Gene therapy is back into play after a decade-long failed deliveries. 2017 was a golden year in gene therapy arena, various companies are aggressively developing gene therapy based treatments targeting life-threatening indications. Spark therapeutics got USFDA approval for the first-ever gene therapy based blindness treatment Luxturna. The therapy will help patients with a faulty gene in DNA i.e. RPE65 gene. The company will insert a functional RPE65 gene into the patients DNA to replace the defective gene resulting in vision restoration. It’s a one-time treatment with a hefty price tag of around USD 1 million making it a long shot for the patients. Luxturna got the ap...
