Central Nervous System

Spinal muscular atrophy is a genetic disorder characterised by weakness and wasting (atrophy) of skeletal muscles, used for movement. Loss of specialised nerve cells, called motor neurons which controls muscle movement, results in weakness of muscles. It mostly affects proximal muscles and respiratory muscles. SMA is one of the most common causes of infant death and mobility impairment.Spinal muscular atrophy has no cure, but treatments can improve some symptoms and in some cases, help the patients live longer. Researchers are working robustly to find new ways to fight the disease. Spinraza, manufactured by Biogen is the only approved drug for the treatment of Spinal ...