"Research is the only hope for families affected by Duchenne muscular dystrophy, and every step forward is a step closer to a cure."
Duchenne Muscular Dystrophy (DMD) is a severe form of muscular dystrophy characterized by progressive muscle degeneration and weakness. It is a rare disorder, but it is one of the most common genetic conditions, affecting roughly 1 in every 3,500 male births worldwide. Recent advancements in research and treatment have significantly improved the outlook for patients with DMD. In 2023, the total number of prevalent Duchenne Muscular Dystrophy cases across the 7MM (the US, EU5, and Japan) was approximately 31K. The United States had t...
