Duchenne muscular dystrophy (DMD) is a severe genetic disorder primarily affecting young boys between the ages of two and three. As per Delveinsight’s estimates, there were approximately 16K DMD patients in 2023 in the United States, with ˜75% of the patients below the age of 15. This condition leads to progressive muscle degeneration, initially presenting as muscle weakness and difficulties with movement. DMD is caused by mutations in the gene responsible for producing dystrophin, a crucial protein for muscle stability and function.
Estimated Patient Burden of DMD (2023)
USA
˜16,000
EU4+UK
˜12,000
Japan
˜3,50...
