How is a Rare disease defined? Well, it depends on the geography in question, since there is no universal definition, even so, the definition revolves around the point of prevalence or incidence of rare disease. If we talk about the United States, a rare disease affects fewer than 200,000 people (Orphan Drug Act). While in the European Union, a rare disease is a disease that affects fewer than 1 in 2,000 people. However, despite the changing attributes in the definition, there is one common ground every country faces‒challenges in mapping the patient pool, R&D, development of therapies, and investments & funding. Let us have a look at the unique challenges tha...
