Rare Indication

Mar 01, 2021

Rare diseases–also go by the name Orphan diseases–are the conditions that do not affect many individuals out there in one particular geographic area. Going deeper into the definition, it also means a lesser patient pool for a therapy developed for one identified rare condition. Unfavorable drug uptake would automat...

Dec 13, 2019

AI-driven treatment approach and growing Fragile X Syndrome market size Healx Pharma has recently partnered with Boehringer Ingelheim to advance the treatment market and invest in R&D related to rare neurological disorders. Under the deal signed, Healx Artificial Intelligence (AI) drug discovery platfo...

Feb 28, 2019

A rare disease is any disease that affects a small percentage of the population. In some parts of the world, an orphan disease is a rare disease whose rarity means there is a lack of a market large enough to gain support and resources for discovering treatments for it, except by the government g...

Aug 18, 2017

Friedreich's ataxia is one of the rare inherited nervous system disorder which causes movement abnormalities like slowed voluntary movement leading to gait disturbance and decreased coordination. It usually begins in childhood and leads to impaired muscle coordination (ataxia) that worsens gradually with time. In 18...